Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease.
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Guidelines for the restart of imiglucerase in patients with Gaucher disease: recommendations from the European Working Group on Gaucher disease.
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Force majeure: therapeutic measures in response to restricted supply of imiglucerase (Cerezyme) for patients with Gaucher disease.
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The role of the iminosugar N-butyldeoxynojirimycin (miglustat) in the management of type I (non-neuronopathic) Gaucher disease: a position statement.
Cox TM, Aerts JM, Andria G, et al. J Inherit Metab Dis. 2003;26(6):513-26.
Management of neuronopathic Gaucher disease: a European consensus.
Vellodi A, Bembi B, de Villemeur et al. J Inherit Metab Dis. 2001 Jun;24(3):319-27.